sickle cell disease

While faster reviews could bring life-saving treatments to patients sooner, compressed timelines could also limit regulatory scrutiny and strain FDA resources.

Discover new treatments for sickle cell disease, including gene therapy, CRISPR, and novel drugs that offer hope for patients worldwide.

Currently, the only cure for alpha thalassemia is a bone marrow transplant, but the success of gene therapies for related conditions points to a potential new cure.

Researchers correcting the genetic causes of disease at the DNA or RNA level make their cases.

Red blood cells may play a role in COVID-19 and other infections.

A biopharmaceutical company established a new method for isolating and editing hematopoietic stem cells from patients to provide stem cell therapies for diseases such as sickle cell disease.