Gairdner Awards 2024 honor pioneering work in health research
This year’s laureates have made groundbreaking discoveries from unlocking the secrets of DNA to fighting enteric diseases and cancer.
pediatrics
Pigs provide a better model for Batten disease
A new porcine model for the rare neurological disorder CLN3 Batten disease more faithfully recreates human symptoms and could accelerate drug development.
Neonatal drug development comes out of the Dark Ages
Left out of clinical trials for years, preterm infants have very few drugs developed just for them. Regulators, industry, and neonatologists plan to fix that.
An in utero stem cell transplant for alpha thalassemia
Alpha thalassemia was once a fatal diagnosis. Now, a clinical trial tests if administering a mother’s stem cells in utero may cure kids before they’re born.
A spoonful of oleogel helps the medicine go down
Scientists developed a gel formulation that makes swallowing medicines easier.
For neurological disorders, milk-based therapies are on the way
From peptides to sugars to lipids, researchers investigate milk as an untapped source of therapeutics for conditions as diverse as anxiety and infant brain injury.
Ultra-rare childhood fevers are no match for this scientist
Recurrent high fevers in children are always worrying, but by studying patient cells, immunologist Lori Broderick hopes to reveal the underlying causes of these disorders.
Tracing autoimmunity’s roots to babies and bacteria
Microbiome researchers seek to predict and prevent autoimmunity in infants.
