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lysosomal storage disorders
lysosomal storage disorders
| 3 min read
by
Lori Lesko
The outlook is BRIGHT for Fabry disease
Protalix and Chiesi share encouraging data from Phase 3 trial evaluating pegunigalsidase alfa in Fabry disease
Articles
| 2 min read
by
Mel J. Yeates
Moving against mucopolysaccharidosis
EMA grants Orphan Drug designation to JR-171 for the treatment of mucopolysaccharidosis type I
News
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