Moderna’s path to mRNA therapies for rare metabolic disorders
Paolo Martini leads the biotech company’s rare disease research program with the hope of developing the very first treatments for genetic metabolic disorders.
genetic disease
The chronic hiccup chronicles
Researchers and patients developed unexpected and innovative solutions to a mysterious disease that appears as little more than a hiccup.
A gene therapy hope for halting Huntington’s disease
A one-time gene therapy aims to stop Huntington's disease at its source. But first, it has to survive clinical trials.
The intricate design of a fundamental filter protein
A collaboration of nephrologists and biochemists created the first structure of “megalin,” a critical protein in kidney and brain disorders.
Cell Therapy Advances: From Benchtop to Bedside
LIVE May 12th, 2022 at 2:30 PM
Discover the most current cell therapy research and the challenges of translating them into the clinic.
Discover the most current cell therapy research and the challenges of translating them into the clinic.
