adeno-associated viral vectors (AAVs)

Researchers created an improved method for assays that detect viral vectors in a patient’s blood or urine. It’s used to ensure that bystanders will not be exposed.

A gene therapy targeting excitatory neurons significantly reduced seizures in a mouse model of the most common cause of child epilepsy.

Experts discussed the major hurdles of AAV gene therapy, including immunogenicity, vector design, and AAV variability.