adeno-associated viral vectors (AAVs)
| 5 min read
After a decade of promise, AAV therapies are now confronting economic, clinical, and regulatory hurdles.
| 6 min read
Via a unique regulatory route in the UK, scientists found that a gene therapy restored vision in young kids with a very rare and severe retinal dystrophy.
| 3 min read
New dual AAV vector delivery overcomes challenges in delivering large genes.
| 3 min read
The gene therapy treats the rare genetic disease AADC deficiency by delivering a functional gene into the brain.
| 5 min read
Researchers created an improved method for assays that detect viral vectors in a patient’s blood or urine. It’s used to ensure that bystanders will not be exposed.
| 4 min read
A gene therapy targeting excitatory neurons significantly reduced seizures in a mouse model of the most common cause of child epilepsy.
| 6 min read
Experts discussed the major hurdles of AAV gene therapy, including immunogenicity, vector design, and AAV variability.
Page 1 of 1 - 7 Total Items
