CRISPR editing for treating Duchenne muscular dystrophy
Researchers are using CRISPR gene editing to restore function of the mutant protein that causes Duchenne muscular dystrophy, a genetic disease that causes muscle degeneration.
Rare & Genetic Diseases
CRISPR-based muscular dystrophy therapy
An engineer turned biology researcher co-founded a bio-pharma start-up with the goal of using CRISPR to reverse the mutation causing the degenerative muscle disorder Duchenne muscular dystrophy.
In Vivo CRISPR Gene Editing for Genetic Disorders
LIVE October 25th, 2021 at 1:00 PM ET
Delivering CRISPR cargo in vivo to treat disease-causing DNA mutations
Delivering CRISPR cargo in vivo to treat disease-causing DNA mutations
Understanding bacteriophages
Ultra-microscopic viruses that selectively target and kill bacteria may mitigate antimicrobial resistance.
Genetic studies of rare undiagnosed diseases take flight with model organisms
Researchers use fruit flies to figure out how genetic mutations disrupt biology and how drugs might reverse these effects.
CRISPR advances cardiovascular disease research
CRISPR gene editing directly and indirectly drives advances in cardiovascular disease therapeutic development.
Keolu Fox revises historical narratives with genome data
A native Hawaiian, anthropologist, and genome scientist, Keolu Fox investigates how mutations found in indigenous populations contribute to human health and emphasizes the importance of considering who benefits from research involving indigenous genomes.
Small but Powerful: Small Molecule Drug Design
LIVE August 26th, 2021 at 11:00 AM ET
In this webinar, experts will discuss new approaches to identify small therapeutic candidates targeting diabetes and Alzheimer’s disease.
On Target: Understanding Base Editors
LIVE July 28th, 2021 at 2:30 PM ET
In this webinar, experts will discuss cytosine and adenosine base-editors to introduce point mutations in DNA strands without creating a breakpoint, and opportunities and considerations for using them.
In this webinar, experts will discuss cytosine and adenosine base-editors to introduce point mutations in DNA strands without creating a breakpoint, and opportunities and considerations for using them.
Addison’s disease patients may retain adrenal cortex function
Sævik measures corticosteroid levels in people with Addison’s disease to challenge the pervasive idea that these patients lose all adrenal cortex function as their disease progresses.
