Gene therapy offers promise for treating complex diseases like genetic disorders and cancer. Researchers are exploring a variety of gene editing approaches, such as small interfering RNA and CRISPR, and delivery systems like viral vectors and lipid nanoparticles, while tackling challenges in safety and efficacy.
Download this compendium from Drug Discovery News and its life sciences supporter, Bio-Rad, to explore the latest strategies and expert insights on improving gene therapy delivery, minimizing immunogenicity risks, and enhancing quality control.
Here’s a sneak peek at what’s inside
- Poster: corralling CRISPR into cells
- Webinar: overcoming the challenges of gene therapy
- Milestone article: droplet digital PCR and its impact on gene therapy
