A drawing of a person with a healthy arm muscle is shown on the left. An arrow points to a drawing of a person with a dystrophied muscle in a circle on the right.

Dystrophied muscle

Shannon Herring

Infographic: CRISPR editing for treating Duchenne muscular dystrophy

Researchers are using CRISPR gene editing to restore function of the mutant protein that causes Duchenne muscular dystrophy, a genetic disease that causes muscle degeneration.
Natalya Ortolano, PhD Headshot
| 1 min read

Duchenne muscular dystrophy is a rare genetic disorder that causes muscles to slowly break down over time, leading to symptoms such as difficulty walking. Dysfunction of the muscle stabilizing protein dystrophin is the primary cause of the disease. The biotech company MyoGeneBio uses CRISPR gene editing to restore partial function of dystrophin to minimize symptoms and slow the progression of disease.

Download the infographic: CRISPR editing for treating Duchenne muscular dystrophy

By Natalya Ortolano, PhD
illustrated by Shannon herring

About the Author

  • Natalya Ortolano, PhD Headshot

    Natalya received her PhD in from Vanderbilt University in 2021; she joined the DDN team the same week she defended her thesis. Her work has been featured at STAT News, Vanderbilt Magazine, and Scientific American. As an assistant editor, she writes and edits online and print stories on topics ranging from cows to psychedelics. Outside of work you can probably find her at a concert in her hometown Nashville, TN.

Related Topics

Published In

October 2021 Issue, Drug Discovery News
Volume 17 - Issue 10 | October 2021

October 2021

October 2021 Issue

Loading Next Article...
Loading Next Article...
Subscribe to Newsletter

Subscribe to our eNewsletters

Stay connected with all of the latest from Drug Discovery News.

Subscribe

Sponsored

Gold circles with attached purple corkscrew shapes represent gold nanoparticles against a black background.

Driving gene therapy with nonviral vectors 

Learn why nonviral vectors are on the rise in gene therapy development.
A 3D digital illustration of a viral spike protein on a cell surface, surrounded by colorful, floating antibodies in the background

Milestone: Leapfrogging to quantitative, high throughput protein detection and analysis

Researchers continuously push the boundaries of what’s possible with protein analysis tools.
Blue cancer cells attached to a cellular surface against a bright blue background in a 3D rendering of a cancer infection.

Advancing immuno-oncology research with cellular assays

Explore critical insights into immunogenicity and immunotoxicity assays for cancer therapies.
Drug Discovery News November 2024 Issue
Latest IssueVolume 20 • Issue 6 • November 2024

November 2024

November 2024 Issue

Explore this issue