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Rare & Genetic Diseases
| 7 min read
Achieving higher accuracy and depth in bottom-up proteomics involves navigating a multifaceted process with various steps and challenges.
| 3 min read
Epilepsy onset and seizure severity are linked to variants in the SCN2A gene, potentially leading to improved diagnostics and treatments.
| 5 min read
BioSpring and Pantherna agree on strategic cooperation in the field of genome editing
| 4 min read
A new method called “REVeRT” expands the capabilities of gene delivery platforms by transporting larger genes than previously possible.
| 5 min read
Biologics like monoclonal antibodies and mRNA vaccines are complex drugs. Yongchao Su uses biophysical tools and innovative strategies to understand them better.
| 5 min read
Researchers created an improved method for assays that detect viral vectors in a patient’s blood or urine. It’s used to ensure that bystanders will not be exposed.
| 10 min read
People with achromatopsia have never seen color. Restorative gene therapies have had mixed success, leaving researchers wondering why.
| 5 min read
The durability and capacity to boost protein expression of circular RNA makes it a promising candidate for next-generation vaccines and gene therapies.
Spatial transcriptomics technologies unveil a goldmine of biological information.
| 1 min read
Cutting-edge DNA synthesis technology propels scientific advancements and drug discoveries forward at unprecedented speeds.
| 3 min read
By watching brain organoids develop, researchers observed surprising abnormalities caused by mutations in a gene related to early-onset Alzheimer’s disease.
| 4 min read
A gene therapy targeting excitatory neurons significantly reduced seizures in a mouse model of the most common cause of child epilepsy.
