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Rare & Genetic Diseases

| 3 min read
Most people have a soft spot for orphans. These unfortunate souls, often depicted with unusually large and needy eyes, tug at the heartstrings.
Such has not always been the case in the pharmaceutical industry, where an orphan is a treatment for a rare disease that occurs in fewer than 200,000 people in the United States, as defined by the FDA’s Orphan Drug Act, passed in 1983.




