With a boost from beta, alpha thalassemia gene therapies blossom
Currently, the only cure for alpha thalassemia is a bone marrow transplant, but the success of gene therapies for related conditions points to a potential new cure.
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Glowing hearts reveal sex differences in response to stress
Glowing hearts reveal sex differences in response to stress
Researchers found that male and female mouse hearts respond differently to stress by monitoring chemical and electrical signaling simultaneously for the first time.
A gene therapy hope for halting Huntington’s disease
A gene therapy hope for halting Huntington’s disease
A one-time gene therapy aims to stop Huntington's disease at its source. But first, it has to survive clinical trials.
2024 Breakthrough Prizes in Life Sciences
2024 Breakthrough Prizes in Life Sciences
This year’s Breakthrough Prizes honor advances in CAR T cancer therapies, cystic fibrosis, and Parkinson’s disease.
A vision of the future: Stem cells offer hope for retinal degeneration
A vision of the future: Stem cells offer hope for retinal degeneration
Cell therapies derived from stem cells could one day prevent vision loss or even restore sight in retinal degenerative disease.
Rewiring cell communication to treat melanoma
Rewiring cell communication to treat melanoma
Exosomes show encouraging results for treating melanoma, offering potential benefits for targeted drug delivery and immunotherapy
Advancing immune forces at the tumor frontlines
Advancing immune forces at the tumor frontlines
Epigenetic therapies revive the immune cell offensive in immunotherapy resistant tumors.
